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세계의 레트증후군 시장 보고서(2025년)
Rett Syndrome Global Market Report 2025
상품코드 : 1760705
리서치사 : The Business Research Company
발행일 : On Demand Report
페이지 정보 : 영문 175 Pages
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한글목차

레트증후군 시장 규모는 향후 몇 년 동안 강력한 성장세를 보일 것으로 예상되며, 2029년까지 9.9%의 CAGR로 10억 2,000만 달러에 달할 것으로 예상됩니다. 예측 기간 동안 예상되는 성장의 원동력은 레트증후군의 유병률 증가, 연구 자금 강화, 질병 변형 치료에 대한 수요 증가, 생명공학 기업의 투자 확대, 혁신적인 치료법 파이프라인의 확대 등입니다. 이 기간 동안 예상되는 주요 동향으로는 유전자 치료의 발전, 신경염증 연구의 발전, 신약개발 과정에 인공지능(AI)의 통합, 증상 관리 장치의 개선, 본 질환의 이해와 치료에 대한 지속적인 연구 개발 등이 있습니다.

유전성 질환의 유병률 증가는 향후 몇 년 동안 레트증후군 시장의 성장에 크게 기여할 것으로 예상됩니다. 유전성 질환은 부모로부터 자녀에게 유전되는 유전자 변이로 인한 질환으로 낭포성섬유증, 겸상 적혈구 빈혈, 혈우병, 헌팅턴병과 같은 질환이 포함됩니다. 이러한 질환의 증가에 기여하는 두드러진 요인은 부모의 나이가 많을수록 유전자의 돌연변이가 유아에게 전달될 위험이 높아진다는 것입니다. 레트증후군은 특히 메틸 CpG 결합 단백질 2(MECP2) 유전자 돌연변이의 영향을 조명함으로써 유전성 질환을 이해하는 데 중요한 모델이 되고 있으며, MECP2는 신경 발달 메커니즘에 대한 지식을 증진시키고, 유사한 질환에 대한 유전학적 표적 치료 연구를 지원하고 있습니다. 예를 들어, 2024년 호주의 비영리 단체인 퍼스 혈액 연구소(Perth Blood Lab)는 혈우병 진단 건수가 2021년 23만 3,577명에서 2022년 25만 7,146명으로 증가할 것이라고 보고했습니다. 결과적으로 유전성 질환의 유병률 증가는 렛트 증후군 시장의 성장을 견인하고 있습니다.

레트증후군 시장의 주요 기업들은 질병의 근본적인 유전적 원인을 해결하고 MECP2의 기능을 회복시켜 증상을 완화하거나 회복시킬 수 있는 후생유전학적 치료법을 포함한 혁신적인 치료법 개발에 집중하고 있습니다. 후생유전학적 치료는 DNA 메틸화, 히스톤 변형, RNA 조절 등의 메커니즘을 표적으로 삼아 근본적인 DNA 서열을 바꾸지 않고 유전자 발현에 영향을 미치는 것을 목표로 합니다. 예를 들어, 2024년 5월 미국 생명공학 기업 Unravel Biosciences Inc.는 미국 식품의약국(FDA)으로부터 볼리노스타트(RVL-001)를 레트증후군 치료제로 승인받았습니다. 아세틸화 효소(HDAC)를 억제하여 신경세포에서 적절한 유전자 발현을 회복시키는 작용을 합니다. 이러한 후생유전학적 조절은 MECP2 돌연변이의 영향을 상쇄하고 신경 기능을 향상시킬 수 있습니다.

목차

제1장 주요 요약

제2장 시장 특징

제3장 시장 동향과 전략

제4장 시장 - 금리, 인플레이션, 지정학, 무역 전쟁과 관세, 코로나와 회복이 시장에 미치는 영향을 포함한 거시경제 시나리오

제5장 세계의 성장 분석과 전략 분석 프레임워크

제6장 시장 세분화

제7장 지역별·국가별 분석

제8장 아시아태평양 시장

제9장 중국 시장

제10장 인도 시장

제11장 일본 시장

제12장 호주 시장

제13장 인도네시아 시장

제14장 한국 시장

제15장 서유럽 시장

제16장 영국 시장

제17장 독일 시장

제18장 프랑스 시장

제19장 이탈리아 시장

제20장 스페인 시장

제21장 동유럽 시장

제22장 러시아 시장

제23장 북미 시장

제24장 미국 시장

제25장 캐나다 시장

제26장 남미 시장

제27장 브라질 시장

제28장 중동 시장

제29장 아프리카 시장

제30장 경쟁 구도와 기업 개요

제31장 기타 주요 기업과 혁신적 기업

제32장 세계의 시장 경쟁 벤치마킹과 대시보드

제33장 주요 인수합병

제34장 최근의 시장 동향

제35장 시장 잠재력이 높은 국가, 전략

제36장 부록

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영문 목차

영문목차

Rett syndrome is a rare genetic neurological disorder that primarily affects females and leads to significant cognitive and motor impairments. It generally emerges after an initial period of normal development and is caused by mutations in the methyl-CpG binding protein 2 (MECP2) gene, which plays a vital role in brain function. Common symptoms include the loss of purposeful hand use, loss of spoken language, and repetitive behaviors such as hand-wringing.

The primary types of rett syndrome are classic Rett syndrome and atypical Rett syndrome. Classic Rett syndrome is a rare condition that predominantly affects girls and is marked by normal early development followed by a regression in motor and communication abilities due to MECP2 gene mutations. The condition typically progresses through four stages stage I (early onset), stage II (rapid destruction), stage III (plateau), and stage IV (late motor deterioration). Treatment approaches include medications, physical therapy, occupational therapy, speech and language therapy, and other supportive interventions. Diagnosis is commonly confirmed through blood work, genetic testing, and other methods, with care provided in settings such as hospitals, specialty clinics, homecare, and other healthcare facilities.

The rett syndrome market research report is one of a series of new reports from The Business Research Company that provides rett syndrome market statistics, including the rett syndrome industry's global market size, regional shares, competitors with the rett syndrome market share, detailed rett syndrome market segments, market trends and opportunities, and any further data you may need to thrive in the rett syndrome market. This rett syndrome market research report delivers a complete perspective of everything you need, with an in-depth analysis of the current and future scenarios of the industry.

The rett syndrome market size has grown strongly in recent years. It will grow from $0.63 billion in 2024 to $0.70 billion in 2025 at a compound annual growth rate (CAGR) of 10.2%. The growth observed during the historic period can be attributed to an increase in clinical trials, heightened awareness among healthcare professionals, the expansion of patient advocacy and support networks, the rising adoption of digital health technologies, and a stronger focus on orphan drug development incentives.

The rett syndrome market size is expected to see strong growth in the next few years. It will grow to $1.02 billion in 2029 at a compound annual growth rate (CAGR) of 9.9%. The anticipated growth in the forecast period is expected to be driven by the increasing prevalence of Rett syndrome, enhanced research funding, rising demand for disease-modifying treatments, greater investment by biotechnology companies, and an expanding pipeline of innovative therapies. Key trends projected for this period include progress in gene therapy, advancements in neuroinflammation research, the integration of artificial intelligence (AI) in drug discovery processes, improvements in symptom management devices, and ongoing developments in the understanding and treatment of the syndrome.

The increasing prevalence of inherited disorders is anticipated to contribute significantly to the growth of the rett syndrome market in the years ahead. Inherited disorders are conditions that result from genetic mutations passed down from parents to their offspring, and include diseases such as cystic fibrosis, sickle cell anemia, hemophilia, and Huntington's disease. A notable factor contributing to the rise in these conditions is advanced parental age, which heightens the risk of genetic mutations being transmitted to children. Rett syndrome serves as a critical model for understanding inherited disorders by shedding light on the impact of mutations, particularly in the methyl-CpG-binding protein 2 (MECP2) gene. It advances the knowledge of neurodevelopmental mechanisms and supports the exploration of genetically targeted therapies for similar conditions. For example, in 2024, the Perth Blood Institute, an Australian non-profit organization, reported an increase in hemophilia diagnoses from 233,577 individuals in 2021 to 257,146 in 2022. Consequently, the growing prevalence of inherited disorders is propelling the expansion of the rett syndrome market.

Key players in the rett syndrome market are concentrating on the development of innovative treatments, including epigenetic therapies, to address the fundamental genetic causes of the disorder, restore MECP2 function, and potentially alleviate or reverse symptoms. Epigenetic therapies aim to influence gene expression without altering the underlying DNA sequence by targeting mechanisms such as DNA methylation, histone modification, or RNA regulation. For example, in May 2024, Unravel Biosciences Inc., a U.S.-based biotechnology firm, received approval from the U.S. Food and Drug Administration (FDA) for vorinostat (RVL-001) as a potential treatment for Rett syndrome. RVL-001 functions by inhibiting histone deacetylases (HDACs), restoring appropriate gene expression in neurons. This form of epigenetic modulation helps to offset the effects of the MECP2 mutation, with the potential to enhance neurological function.

In December 2024, ProQR Therapeutics N.V., a biotechnology company based in the Netherlands, expanded its partnership with the Rett Syndrome Research Trust (RSRT) to advance RNA editing therapies focused on MECP2 mutations, particularly the R270X mutation, through its Axiomer platform. This collaboration aims to accelerate the development of AX-2402 for entry into clinical trials, offering a promising disease-modifying treatment for Rett syndrome. The Rett Syndrome Research Trust is a U.S.-based nonprofit organization dedicated to supporting and expediting research efforts to find a cure for Rett syndrome.

Major players in the rett syndrome market are UNC Hospital, Boston Children's Hospital, Vanderbilt Health, Jazz Pharmaceuticals plc, Cincinnati Children's Hospital Medical Center, Sarepta Therapeutics Inc., Ionis Pharmaceuticals Inc., Acadia Pharmaceuticals Inc., Regenxbio Inc., Beam Therapeutics Inc., Shape Therapeutics Inc., Unravel Biosciences Inc., Neuren Pharmaceuticals Limited, Taysha Gene Therapies, Prilenia Therapeutics Inc., Anavex Life Sciences Corp, Neurogene Inc., Neurolixis Inc., DepYmed Inc., and Neurotech International Limited.

North America was the largest region in the rett syndrome market in 2024. Asia Pacific is expected to be the fastest-growing region in the forecast period. The regions covered in rett syndrome report are Asia-Pacific, Western Europe, Eastern Europe, North America, South America, Middle East and Africa.

The countries covered in the rett syndrome market report are Australia, Brazil, China, France, Germany, India, Indonesia, Japan, Russia, South Korea, UK, USA, Canada, Italy, Spain.

The rett syndrome market consists of revenues earned by entities by providing services such as diagnostic testing, genetic counseling, specialized therapeutic interventions, ongoing medical care, and support for affected individuals. The market value includes the value of related goods sold by the service provider or included within the service offering. The rett syndrome market also includes sales of medical devices, nutritional supplements, assistive communication devices, adaptive equipment, and therapeutic tools. Values in this market are 'factory gate' values, that is, the value of goods sold by the manufacturers or creators of the goods, whether to other entities (including downstream manufacturers, wholesalers, distributors, and retailers) or directly to end customers. The value of goods in this market includes related services sold by the creators of the goods.

The market value is defined as the revenues that enterprises gain from the sale of goods and/or services within the specified market and geography through sales, grants, or donations in terms of the currency (in USD, unless otherwise specified).

The revenues for a specified geography are consumption values that are revenues generated by organizations in the specified geography within the market, irrespective of where they are produced. It does not include revenues from resales along the supply chain, either further along the supply chain or as part of other products.

Rett Syndrome Global Market Report 2025 from The Business Research Company provides strategists, marketers and senior management with the critical information they need to assess the market.

This report focuses on rett syndrome market which is experiencing strong growth. The report gives a guide to the trends which will be shaping the market over the next ten years and beyond.

Reasons to Purchase

Where is the largest and fastest growing market for rett syndrome ? How does the market relate to the overall economy, demography and other similar markets? What forces will shape the market going forward? The rett syndrome market global report from the Business Research Company answers all these questions and many more.

The report covers market characteristics, size and growth, segmentation, regional and country breakdowns, competitive landscape, market shares, trends and strategies for this market. It traces the market's historic and forecast market growth by geography.

The forecasts are made after considering the major factors currently impacting the market. These include the Russia-Ukraine war, rising inflation, higher interest rates, and the legacy of the COVID-19 pandemic.

Scope

Subsegments

Table of Contents

1. Executive Summary

2. Rett Syndrome Market Characteristics

3. Rett Syndrome Market Trends And Strategies

4. Rett Syndrome Market - Macro Economic Scenario Including The Impact Of Interest Rates, Inflation, Geopolitics, Trade Wars and Tariffs, And Covid And Recovery On The Market

5. Global Rett Syndrome Growth Analysis And Strategic Analysis Framework

6. Rett Syndrome Market Segmentation

7. Rett Syndrome Market Regional And Country Analysis

8. Asia-Pacific Rett Syndrome Market

9. China Rett Syndrome Market

10. India Rett Syndrome Market

11. Japan Rett Syndrome Market

12. Australia Rett Syndrome Market

13. Indonesia Rett Syndrome Market

14. South Korea Rett Syndrome Market

15. Western Europe Rett Syndrome Market

16. UK Rett Syndrome Market

17. Germany Rett Syndrome Market

18. France Rett Syndrome Market

19. Italy Rett Syndrome Market

20. Spain Rett Syndrome Market

21. Eastern Europe Rett Syndrome Market

22. Russia Rett Syndrome Market

23. North America Rett Syndrome Market

24. USA Rett Syndrome Market

25. Canada Rett Syndrome Market

26. South America Rett Syndrome Market

27. Brazil Rett Syndrome Market

28. Middle East Rett Syndrome Market

29. Africa Rett Syndrome Market

30. Rett Syndrome Market Competitive Landscape And Company Profiles

31. Rett Syndrome Market Other Major And Innovative Companies

32. Global Rett Syndrome Market Competitive Benchmarking And Dashboard

33. Key Mergers And Acquisitions In The Rett Syndrome Market

34. Recent Developments In The Rett Syndrome Market

35. Rett Syndrome Market High Potential Countries, Segments and Strategies

36. Appendix

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