니만피크병 C형 치료 시장 보고서(2025년)
Niemann-Pick Disease Type C Treatment Global Market Report 2025
상품코드 : 1751057
리서치사 : The Business Research Company
발행일 : On Demand Report
페이지 정보 : 영문 175 Pages
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한글목차

니만피크병 C형 치료 시장 규모는 향후 몇 년간 강력한 성장이 전망됩니다. 유전자 치료의 인기가 높아지고, 유전자 치료의 현저한 진보에 기인하고 있습니다. 이 기간의 주요 동향으로는 기술의 진보, 라이소좀 저장 장애에 대한 맞춤형 의료의 대두, 유전자·분자 연구의 진전, 바이오테크놀러지의 비약적 진보, 혁신적 치료제의 개발 등을 들 수 있습니다.

알츠하이머병의 유병률 증가는 니만피크병 C형 치료 시장의 확대를 가속할 것으로 예측됩니다. 박질의 얽힘이 축적되어 인지기능의 저하, 기억력의 저하, 일상생활기능의 장애를 일으키며, 결국 중증의 치매와 신경퇴행에 이르는 것이 특징입니다. 세계 인구의 고령화에 의한 것이 크고 특히 선진국에서는 평균 수명이 연장됨에 따라 알츠하이머 병과 같은 노화와 관련된 질병의 위험도 상승하고 있습니다. NPC 치료는 리소좀 저장 장애와 지질 대사 기능 장애에 대한 인사이트를 제공함으로써 알츠하이머병 연구에 기여합니다. Alzheimer's Society는 영국에서 2024년에 98만 2천명이 치매를 앓고, 3분의 1 이상이 미진단이라고 추정하고 있습니다. 이 수는 2040년까지 140만명에 이를 것으로 예상되고 있습니다.

니만피크병 C형 치료 시장의 주요 기업은 질병의 진행을 늦추고 환자의 예후를 개선하는 것을 목적으로 한 신경보호치료 등의 혁신적인 치료법의 개발에 주력하고 있습니다. 신경 퇴행성 질환과 같은 신경 기능을 유지하는 것을 목표로 합니다. 단독 치료제인 AQNEURSA(레바세틸류신)의 승인을 받았습니다. AQNEURSA는 움직임, 인지, 일상생활에 영향을 미치는 이 드문 라이소좀 저장장애로 고통받는 사람들에게 대망의 치료 옵션을 제공합니다.

목차

제1장 주요 요약

제2장 시장 특징

제3장 시장 동향과 전략

제4장 시장 - 금리, 인플레이션, 지정학, 무역전쟁과 관세, 코로나 태와 회복이 시장에 미치는 영향을 포함한 거시경제 시나리오

제5장 세계의 성장 분석과 전략 분석 프레임워크

제6장 시장 세분화

제7장 지역별/국가별 분석

제8장 아시아태평양 시장

제9장 중국 시장

제10장 인도 시장

제11장 일본 시장

제12장 호주 시장

제13장 인도네시아 시장

제14장 한국 시장

제15장 서유럽 시장

제16장 영국 시장

제17장 독일 시장

제18장 프랑스 시장

제19장 이탈리아 시장

제20장 스페인 시장

제21장 동유럽 시장

제22장 러시아 시장

제23장 북미 시장

제24장 미국 시장

제25장 캐나다 시장

제26장 남미 시장

제27장 브라질 시장

제28장 중동 시장

제29장 아프리카 시장

제30장 경쟁 구도와 기업 프로파일

제31장 기타 주요 기업 및 혁신 기업

제32장 세계 시장 경쟁 벤치마킹과 대시보드

제33장 주요 인수합병(M&A)

제34장 최근 시장 동향

제35장 시장의 잠재력이 높은 국가, 부문, 전략

제36장 부록

SHW
영문 목차

영문목차

Niemann-Pick disease type C (NPC) treatment refers to the medical strategies used to manage and slow the progression of Niemann-Pick disease type C, a rare inherited neurodegenerative disorder that impairs the body's ability to metabolize cholesterol and other lipids within cells. Treatment typically involves pharmacological and supportive therapies aimed at reducing neurological symptoms, stabilizing the disease, and improving the quality of life for affected individuals.

Note that the outlook for this market is being affected by rapid changes in trade relations and tariffs globally. The report will be updated prior to delivery to reflect the latest status, including revised forecasts and quantified impact analysis. The report's Recommendations and Conclusions sections will be updated to give strategies for entities dealing with the fast-moving international environment.

The main types of Niemann-Pick disease type C treatment focus on Niemann-Pick disease type C1 and Niemann-Pick disease type C2. Niemann-Pick disease type C1 (NPC1) is a rare, progressive, and fatal lysosomal storage disorder caused by mutations in the NPC1 gene. This leads to impaired cholesterol trafficking within cells, resulting in the accumulation of lipids in lysosomes, and causing severe neurological deterioration such as cognitive decline, motor dysfunction, and organ damage. NPC treatment spans various age groups, including infantile, juvenile, and adult populations, with end-users including hospitals, specialty clinics, and research and academic institutions.

The niemann-Pick disease type C treatment market research report is one of a series of new reports from The Business Research Company that provides niemann-Pick disease type C treatment market statistics, including niemann-Pick disease type C treatment industry global market size, regional shares, competitors with a niemann-Pick disease type C treatment market share, detailed niemann-Pick disease type C treatment market segments, market trends and opportunities, and any further data you may need to thrive in the niemann-Pick disease type C treatment industry. This niemann-Pick disease type C treatment market research report delivers a complete perspective of everything you need, with an in-depth analysis of the current and future scenario of the industry.

The niemann-Pick disease type C treatment market size has grown strongly in recent years. It will grow from $2.68 billion in 2024 to $2.93 billion in 2025 at a compound annual growth rate (CAGR) of 9.2%. The growth observed during the historic period can be attributed to the expansion of healthcare infrastructure, a rising number of cases involving mutations in the NPC1 and NPC2 genes, a growing prevalence of Niemann-Pick disease, increased government funding for research into rare disease treatments, and heightened awareness and advocacy efforts.

The niemann-Pick disease type C treatment market size is expected to see strong growth in the next few years. It will grow to $4.14 billion in 2029 at a compound annual growth rate (CAGR) of 9.1%. The growth projected during the forecast period can be attributed to increasing research and development activities, a growing number of pipeline drugs, a high prevalence of rare diseases, the emerging popularity of gene therapy, and significant advancements in genetic therapies. Key trends during this period include advancements in technology, the rise of personalized medicine for lysosomal storage disorders, progress in genetic and molecular research, breakthroughs in biotechnology, and the development of innovative therapeutics.

The growing prevalence of Alzheimer's disease is expected to accelerate the expansion of the Niemann-Pick disease type C (NPC) treatments market. Alzheimer's disease is a progressive neurodegenerative disorder characterized by the buildup of beta-amyloid plaques and tau protein tangles in the brain, leading to cognitive decline, memory loss, and difficulties with daily functioning, ultimately resulting in severe dementia and neurodegeneration. The increasing prevalence of Alzheimer's disease is largely due to the aging global population. As life expectancy increases, especially in developed nations, the risk of age-related diseases such as Alzheimer's also rises, since advancing age is the most significant known risk factor for the condition. NPC treatment contributes to Alzheimer's disease research by offering insights into lysosomal storage disorders and dysfunctions in lipid metabolism. For example, in May 2024, the Alzheimer's Society, a UK-based health organization, estimated that 982,000 people in the UK were living with dementia in 2024, with more than a third undiagnosed. This number is expected to reach 1.4 million by 2040. Therefore, the growing prevalence of Alzheimer's disease is driving the growth of the Niemann-Pick disease type C treatments market.

Leading companies in the Niemann-Pick disease type C (NPC) treatment market are focusing on developing innovative therapies, such as neuroprotective treatments, aimed at slowing disease progression and improving patient outcomes. Neuroprotective therapies are designed to protect the brain and nervous system from damage or degeneration, with the goal of preserving neurological function in conditions such as neurodegenerative diseases. For example, in September 2024, IntraBio Inc., a US-based biopharmaceutical company, received approval from the United States Food and Drug Administration (FDA) for AQNEURSA (levacetylleucine), the first stand-alone therapy for Niemann-Pick Disease Type C (NPC). This approval followed promising Phase III trial results, showing significant neurological improvements in NPC patients within 12 weeks. AQNEURSA offers a long-awaited treatment option for individuals suffering from this rare lysosomal storage disorder, which affects movement, cognition, and daily function. IntraBio also intends to explore AQNEURSA's potential in treating other neurodegenerative and neurodevelopmental disorders.

In December 2023, Cyclo Therapeutics, Inc., a US-based biotechnology firm, merged with Applied Molecular Transport Inc. for $10.2 million. This merger is aimed at strengthening Cyclo Therapeutics' financial and strategic position by utilizing additional resources, extending its financial runway, and advancing the clinical development and regulatory approval process for Trappsol Cyclo, a potential treatment for Niemann-Pick Disease Type C1 (NPC1). This treatment will undergo the pivotal Phase 3 global study (TransportNPC). Applied Molecular Transport Inc. is a US-based clinical-stage biopharmaceutical company.

Major players in the niemann-pick disease type c treatment market are Merck & Co. Inc., Mayo Clinic, Boston Children's Hospital, Cincinnati Children's Hospital Medical Center, Mallinckrodt Pharmaceuticals, Myriad Genetics Inc., Rainbow Children's Hospital, CENTOGENE N.V., The Florey Institute of Neuroscience and Mental Health, Insilico Medicine Inc., National Organization for Rare Disorders (NORD), Zevra Therapeutics Inc., Azafaros A.G., IntraBio Inc., National Niemann-Pick Disease Foundation (NNPDF), Bloomsbury Genetic Therapies Ltd., CTD Holdings Inc., Okklo Life Sciences, Vtesse Inc., Cyclo Therapeutics Inc., Mandos Health.

North America was the largest region in the niemann-pick disease type C treatment market in 2024. Asia-Pacific is expected to be the fastest-growing region in the forecast period. The regions covered in niemann-Pick disease type C treatment report are Asia-Pacific, Western Europe, Eastern Europe, North America, South America, Middle East and Africa.

The countries covered in the niemann-Pick disease type C treatment market report are Australia, Brazil, China, France, Germany, India, Indonesia, Japan, Russia, South Korea, UK, USA, Canada, Italy, Spain.

The niemann-Pick disease type C treatment market includes revenues earned by entities through medication management, symptom management, neurological care, liver care, and genetic counseling. The market value includes the value of related goods sold by the service provider or included within the service offering. Only goods and services traded between entities or sold to end consumers are included.

The market value is defined as the revenues that enterprises gain from the sale of goods and/or services within the specified market and geography through sales, grants, or donations in terms of the currency (in USD, unless otherwise specified).

The revenues for a specified geography are consumption values that are revenues generated by organizations in the specified geography within the market, irrespective of where they are produced. It does not include revenues from resales along the supply chain, either further along the supply chain or as part of other products.

Niemann-Pick Disease Type C Treatment Global Market Report 2025 from The Business Research Company provides strategists, marketers and senior management with the critical information they need to assess the market.

This report focuses on niemann-pick disease type c treatment market which is experiencing strong growth. The report gives a guide to the trends which will be shaping the market over the next ten years and beyond.

Reasons to Purchase

Where is the largest and fastest growing market for niemann-pick disease type c treatment ? How does the market relate to the overall economy, demography and other similar markets? What forces will shape the market going forward? The niemann-pick disease type c treatment market global report from the Business Research Company answers all these questions and many more.

The report covers market characteristics, size and growth, segmentation, regional and country breakdowns, competitive landscape, market shares, trends and strategies for this market. It traces the market's historic and forecast market growth by geography.

The forecasts are made after considering the major factors currently impacting the market. These include the Russia-Ukraine war, rising inflation, higher interest rates, and the legacy of the COVID-19 pandemic.

Scope

Table of Contents

1. Executive Summary

2. Niemann-Pick Disease Type C Treatment Market Characteristics

3. Niemann-Pick Disease Type C Treatment Market Trends And Strategies

4. Niemann-Pick Disease Type C Treatment Market - Macro Economic Scenario Including The Impact Of Interest Rates, Inflation, Geopolitics, Trade Wars and Tariffs, And Covid And Recovery On The Market

5. Global Niemann-Pick Disease Type C Treatment Growth Analysis And Strategic Analysis Framework

6. Niemann-Pick Disease Type C Treatment Market Segmentation

7. Niemann-Pick Disease Type C Treatment Market Regional And Country Analysis

8. Asia-Pacific Niemann-Pick Disease Type C Treatment Market

9. China Niemann-Pick Disease Type C Treatment Market

10. India Niemann-Pick Disease Type C Treatment Market

11. Japan Niemann-Pick Disease Type C Treatment Market

12. Australia Niemann-Pick Disease Type C Treatment Market

13. Indonesia Niemann-Pick Disease Type C Treatment Market

14. South Korea Niemann-Pick Disease Type C Treatment Market

15. Western Europe Niemann-Pick Disease Type C Treatment Market

16. UK Niemann-Pick Disease Type C Treatment Market

17. Germany Niemann-Pick Disease Type C Treatment Market

18. France Niemann-Pick Disease Type C Treatment Market

19. Italy Niemann-Pick Disease Type C Treatment Market

20. Spain Niemann-Pick Disease Type C Treatment Market

21. Eastern Europe Niemann-Pick Disease Type C Treatment Market

22. Russia Niemann-Pick Disease Type C Treatment Market

23. North America Niemann-Pick Disease Type C Treatment Market

24. USA Niemann-Pick Disease Type C Treatment Market

25. Canada Niemann-Pick Disease Type C Treatment Market

26. South America Niemann-Pick Disease Type C Treatment Market

27. Brazil Niemann-Pick Disease Type C Treatment Market

28. Middle East Niemann-Pick Disease Type C Treatment Market

29. Africa Niemann-Pick Disease Type C Treatment Market

30. Niemann-Pick Disease Type C Treatment Market Competitive Landscape And Company Profiles

31. Niemann-Pick Disease Type C Treatment Market Other Major And Innovative Companies

32. Global Niemann-Pick Disease Type C Treatment Market Competitive Benchmarking And Dashboard

33. Key Mergers And Acquisitions In The Niemann-Pick Disease Type C Treatment Market

34. Recent Developments In The Niemann-Pick Disease Type C Treatment Market

35. Niemann-Pick Disease Type C Treatment Market High Potential Countries, Segments and Strategies

36. Appendix

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